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  • /content/sustained-long-term-benefit-gene-therapy-sma
  • /neurologyreviews/article/240664/rare-diseases/sustained-long-term-benefit-gene-therapy-sma
  • /pediatricnews/article/240664/rare-diseases/sustained-long-term-benefit-gene-therapy-sma
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  • /neurology/article/240664/rare-diseases/sustained-long-term-benefit-gene-therapy-sma
  • /breast-cancer-icymi/article/240664/rare-diseases/sustained-long-term-benefit-gene-therapy-sma
  • /b-cell-lymphoma-icymi/article/240664/rare-diseases/sustained-long-term-benefit-gene-therapy-sma